캴 ȯڵ (Hemlibra, emicizumab) 1 Ÿ. ȯڵ ġḦ ǰ ǰ ߴٰ Ϻ ȯڵ鿡Լ ӵǾٰ .
̹ ȯڵ Ÿٰ . “ָ̽ ġ 1 ü õ A 캴 ȯ ӻ ġ, ” Haemophilia ο Ǿ.
A 캴 ȯڿ ʼ ܹ FVIII ۿ ϵ ü ġ̴. ġ ܰ踦 Ͽ ϰų ̴µ ֵ Ǿ.
̿ , ǥ ü ȿ ߸ ִ 8 ü A 캴 ȯ ο ̱ εǾ óǰ ִ. ڰ ֻ , Ϲ δ 1ȸ 4ֿ 1ȸ ȴ. ̷ ִ ڰ, Ȥ Ƿ ü 湮Ͽ ؾ ߴ ٸ ġ Ǽ 鿡 ϴ ˷.
ģ (Cochin Hospital) 캴 ġἾʹ ġ ȯڵ ġ 2 Ŀ 1 Ŀ ϴ ȯ α Ͽ. ȯڵ ǰ, ȯڵ νİ ǰ ȭ ΰ ش α Ͽ.
м 2020 6 2021 3 ̿ ġḦ A 캴 38 Ͽ. ȯ 45.5 8 (FVIII) ü ȯڴ . ù° Ϲ ǰ, , ڿ , ܻ ĺ ɷ ǰ Ű Ǿ ̴ 1 ° ȸǿ ٽ Ǿ. EQ-5D-3L Ǿµ, ȯ ̵, ڰ, ϻȰ, ̵, Ҿ 5 ϰ ִ.
ȯڵ ġ 1 (ڹ ܻ ) ũ Ӹ ƴ϶ ϰ ǰ Ǿٰ ߴ. , Ϲ ġ ū ȭ ĺϴ ɷ ߴٰ ߴ.
1 100 ô ǥϴ ǰ ¿ ȯڵ ڽ ǰ 69.6 ϰ ִٰ ߴ. ұϰ EQ-5D-3L ȣϴ ȯڵ ȮεǾ. κ ȯ(73.7%) Ϻ , 13.1% ؽ ߴ. 28(73.7%) ϴ Ÿ.
ٸ κ ȯڰ ϻȰ (89.5%) ϻȰ (71.1%) Ÿ ġῡ . , (44.7%) ̵ ٰ ߴ. Ϻ ȯڴ ߴߴ Ȱ 簳 ִٰ ߰(39.5%), ٸ ȯڴ ο Ȱ ߴٰ ߴ(21.1%). ġḦ 12 ġ ʿ伺 ߴٰ 1/3 ġḦ Ҵٰ ߴ.
̷ ġḦ ϴ ߿ϴٰ ϰ ִ. ڵ 60.5% Ҿ 15 Ϻ, Ȥ ɰ ̱ ߴ.
˷ ұϰ ȯڵ ‘캴 ٸ ȯ ϱ ʹ ʾ’ , ̷ ȯڵ ̳ ûҳ ġḦ ģ Ǿ ̴ ̵ ٸ Ҵٰ .
鿡 ȯ (52.6%) ּ 1ȸ ñ⸦ ġ κ ؾ ˰ ־. , ֿ ۿδ ַ , Ǻ Ǵ ־.
ȯڵ 10 9.1 ġ ư ʹٴ ǻ縦 . ŰƮ 6 3.2 ټ Ǿ.
̹ 뿡 ûϸ, ̴ ȯڵ ϴ ǰ ־. ̷ ߰ Ȯϱ ũ Ⱓ ģ ʿϴٰ ߴ.
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