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[] ߱ BBM-H803 캴 ȯڿ ù
̿(Belief BioMed) 캴 A ȯ ȸ ġ BBM-H803 ӻ迡 ù° 캴 ȯڿ Ǿٰ . ̹ ӻ(CTR20233400) BBM-H8
Ȳ
2024-01-29
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[] 帮 WFH ȸ Ѵ
4 帮忡 쿬(WFH) ȸ 뷫 Դ.WFH ̹ Ȩ ̸ 4 21Ϻ 24ϱ ȸ α ົ(Program at a glance) ߴ.
2024-01-17
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[] ʥ, 9 ġ 'ũ'
캴 9 'ġ' ġ 'ũ' ijٿ 㰡 Ҵ. ̰ ֱٿ ε ġ 'н' ̾ ι°̴. ȭڰ 'ũ(Beqvez)'
2024-01-11
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[] ֵ뺣Ʈ Ʈ, 캴 ġ ''
ݰ 뷮 þ , ̱ ݰ (EHL) ֵ뺣Ʈ(Adynovate, rurioctocog alfa pegol) Ʈ(Eloctate, efmoroctocog al
Ȳ
2024-01-02
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[] н, 캴 ȯ ߰ پ
캴B ġ н(Hemgenix, etranacogene dezaparvovec) , Ǵ ߵ 캴 B ȯ 뷮 ּ 3 Ǵ Ÿ.
Ȳ
2023-12-29
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[] '1ȸ 8' , ȯ а
(Altuviiio, efanesoctocog alfa) XTEND-Kids ӻ迡 κ 캴A ȯƿ θ ӻ ͺ信 1ȸ ġ Ǿٰ ,
Ȳ
2023-12-20
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[] 캴A,B ֻ Ÿø, ̱
1ȸ ֻ Ÿø(marstacimab) ü 캴 A B ȯڿ 㰡ϴ ̱ ǰ ִ. Ÿø ȭ(Pfizer) ̱ ǰǾ౹(FDA) 2024 ,
Ȳ
2023-12-19
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[] ڿڵ 縦
쿬(World Federation of Hemophilia) 5 ڿ Ͽ WFH ڿڵ鿡 Ȩ ߴ. WFH ڿڵ , , ſ
Ȳ
2023-12-11
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[] WFH 2024 ȸ, 帮 ʴ
쿬(World Federation of Hemophilia, WFH) 4 21Ϻ 24ϱ WFH 2024 ȸ ȯ Ŀ´Ƽ ʴϴ ۰ Բ ȸ ֵǴ 帮忡 Ұ Ȩ
Ȳ
2023-12-11
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[] ASC, 8 ġ ӻ
ġ ۵Ǵ , 캴A 2 ġ ASC618 ȿ ϴ 1/2a ӻ ù° ȯ ̷. 2021
Ȳ
2023-12-08
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[] ǰ, 캴A ġῡ
캴A ȯڴ ġ ̿(BioMarin Pharmaceutical) 츮 ΰǰ ǰ ο ̱ Ÿ(Roctavian, valocto
Ȳ
2023-12-04
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[] FDA, Sernova 캴A Ŀġ 㰡
̱ ǰǾ౹(FDA) (Sernova) ο Ƿ Ŀġ ý(Cell Pouch System) 캴A ġ α Ǿǰ ͼҾȯǾ οߴٰ .
Ȳ
2023-12-01
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[] 캴 ȭŰ ܹ S ǥ
9 (FIX) ü ܹ S ǥ ϴ ü ߰ϸ 캴 ȯ ΰ ִ Ҿƿ ȭǴ Ÿ. ̹ PS(ܹ S)
Ȳ
2023-11-29
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[] 캴 ġ ġ ɽƮó
() μ DZⰡ ӻ ߿ ϰ ִ. ŸDZ ؾ ϸ, Ʈ ʸ ̷ ־ ϰ, ÷Ʈ, Ŭ ε Ƹ ־ Ѵ. ̷
Ȳ
2023-11-24
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[] ߱ 캴 ġ, ߰
ֱ ġ ִ (Gritgen Therapeutics) ο ִ ġ GS1191 ߱ ұԸ ӻ迡 캴A ȯ (FVIII) Ȱȭ
Ȳ
2023-11-22
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[] WFH, 2024
쿬(World Federation of Hemophilia) Ȩ 2024 ̿ ȸ: ȯ ˱⡯ 縦 ̶ . WFH ο ġ
Ȳ
2023-11-17
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[] Ÿ, ο EU AAV5 ü Ʈ
캴A ġ Ÿ(Roctavian, valoctocogene roxaparvovec-rvox) ü ȯ ġῡ ݼ ϴµ Ǵ Ʈ AAV5 DetectCDx (EU)
Ȳ
2023-11-17
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[] WFH, 2022 ۷ι ǥ
WFH Ȩ 2022 ۷ι (Annual Global Survey, AGS) Ͽٰ . ۷ι WFH 'θ ġ' ǥ ϴ
Ȳ
2023-11-16
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[] Ʈ 뺸ũ, 캴A ġḦ
Ʈ ̾(Genevant Sciences) 뺸ũ(Novo Nordisk) Ͽ Ʈ (lipid nanoparticle, LNP) ÷ ÷ mRNA megaTAL 캴A
Ȳ
2023-11-16
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[] SerpinPC, 캴B üȯڿ ù ӻ
(Centessa Pharmaceuticals) ȸ ǥڷḦ SerpinPC ȿ ϴ 2b ӻ迡 ü ִ ù° ڰ Ҵٰ ߴ. ߺι ְ ̹(Ant
Ȳ
2023-11-15
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